{"id":836,"date":"2026-07-26T08:40:00","date_gmt":"2026-07-25T23:40:00","guid":{"rendered":"https:\/\/onepress.co.kr\/index.php\/briefing\/2026-07-26-scn2a-personalized-aso-ko\/"},"modified":"2026-07-26T08:48:52","modified_gmt":"2026-07-25T23:48:52","slug":"2026-07-26-scn2a-personalized-aso-ko","status":"publish","type":"briefing","link":"https:\/\/onepress.co.kr\/index.php\/briefing\/2026-07-26-scn2a-personalized-aso-ko\/","title":{"rendered":"\ud658\uc790 \ub450 \uba85\uc744 \uc704\ud574 \uac01\uac01 \ub9cc\ub4e0 \uce58\ub8cc, \ubc1c\uc791\uc774 26%\u00b790% \uc904\uc5c8\ub2e4"},"content":{"rendered":"<p><strong>2026-07-26 08:40 KST<\/strong><\/p>\n<p>SCN2A \uc720\uc804\uc790 \ubcc0\uc774\ub85c \uc911\uc99d \ubc1c\ub2ec\uc131 \ub1cc\uc804\uc99d\uc744 \uc553\ub294 \ub450 \uc544\uc774\uc5d0\uac8c \uac01\uc790\uc758 \ubcc0\uc774 \uc0ac\ubcf8\ub9cc \uaca8\ub0e5\ud55c \uc548\ud2f0\uc13c\uc2a4 \uc62c\ub9ac\uace0\ub274\ud074\ub808\uc624\ud0c0\uc774\ub4dc(ASO)\ub97c \ud22c\uc5ec\ud55c \uacb0\uacfc, 2\ub144 \ub3d9\uc548 \ubc1c\uc791 \ube48\ub3c4\uac00 \uac01\uac01 26%\uc640 90% \uc904\uc5c8\ub2e4.<\/p>\n<p>\ud55c \ud658\uc790\ub294 15\uc138\uc5d0 \ucc98\uc74c \ub3c5\ub9bd \ubcf4\ud589\ud588\uc9c0\ub9cc, \ud658\uc790\uac00 \ub450 \uba85\ubfd0\uc774\uace0 \ubb34\uc791\uc704 \ub300\uc870\uad70\uc774 \uc5c6\ub294 \ucd08\uae30 \uac1c\ubcc4 \uc784\uc0c1\uc2dc\ud5d8\uc774\ub77c\ub294 \ud55c\uacc4\ub3c4 \ud568\uaed8 \ubd10\uc57c \ud55c\ub2e4.<\/p>\n<h2>\uac19\uc740 \ubcd1\uba85\uc774\uc5b4\ub3c4 \uce58\ub8cc\uc81c\ub294 \ub2ec\ub790\ub2e4<\/h2>\n<p>SCN2A \uad00\ub828 \ub1cc\uc804\uc99d\uc740 \uc2e0\uacbd\uc138\ud3ec\uc758 \ub098\ud2b8\ub968 \ud1b5\ub85c\ub97c \ub9cc\ub4dc\ub294 \uc720\uc804\uc790 \ud55c \uc0ac\ubcf8\uc758 \ubcc0\uc774\ub85c \uc2ec\ud55c \ubc1c\uc791\uacfc \ubc1c\ub2ec \uc9c0\uc5f0\uc774 \ub098\ud0c0\ub0a0 \uc218 \uc788\ub2e4. \uc5f0\uad6c\uc9c4\uc740 \uc815\uc0c1 \uc0ac\ubcf8\uc740 \ub0a8\uaca8 \ub450\uace0 \ubcc0\uc774 \uc0ac\ubcf8\uacfc \ud568\uaed8 \uc720\uc804\ub418\ub294 \uc778\uc811 \ud45c\uc9c0\ub97c \uc778\uc2dd\ud558\ub3c4\ub85d \ud658\uc790\ubcc4 ASO\ub97c \ub530\ub85c \uc124\uacc4\ud588\ub2e4.<\/p>\n<p>\ucc99\uc218\uc561\uc5d0 \ub123\uc740 ASO\ub294 DNA\ub97c \uc601\uad6c \uc218\uc815\ud558\uc9c0 \uc54a\uace0 \ubcc0\uc774 \uc0ac\ubcf8\uc758 \ub2e8\ubc31\uc9c8 \uc0dd\uc0b0\uc744 \uc904\uc778\ub2e4. \uadf8\ub798\uc11c \uce58\ub8cc\ub294 2~3\uac1c\uc6d4\ub9c8\ub2e4 \ubc18\ubcf5\ub410\ub2e4.<\/p>\n<h2>\ub450 \uac74\uc758 n-of-1 \uc2dc\ud5d8\uc5d0\uc11c \ub098\uc628 \ubcc0\ud654<\/h2>\n<p>\uce58\ub8cc \uc2dc\uc791 \ub2f9\uc2dc \ud658\uc790\ub294 9\uc138\uc640 14\uc138\uc600\ub2e4. \ubc1c\uc791 \ube48\ub3c4\ub294 \uac01\uac01 26%\uc640 90% \uac10\uc18c\ud588\uace0, \ub450 \ud658\uc790 \ubaa8\ub450 \uc77c\ubd80 \ud56d\uacbd\ub828\uc81c\ub97c \uc904\uc774\uac70\ub098 \uc911\ub2e8\ud588\ub2e4.<\/p>\n<p>\uc5f0\uad6c\uc9c4\uc740 \uc5b8\uc5b4\u00b7\uc6b4\ub3d9\u00b7\uac10\uac01 \ucc98\ub9ac\u00b7\uc801\uc751 \ud589\ub3d9\uc758 \uac1c\uc120\ub3c4 \ubcf4\uace0\ud588\uc73c\uba70, \ub098\uc774\uac00 \ub9ce\uc740 \ud658\uc790\ub294 15\uc138\uc5d0 \ucc98\uc74c \ud63c\uc790 \uac78\uc5c8\ub2e4. \uce58\ub8cc\uc640 \uad00\ub828\ub41c \uc911\ub300\ud55c \uc774\uc0c1\ubc18\uc751\uc740 \ubcf4\uace0\ub418\uc9c0 \uc54a\uc558\ub2e4.<\/p>\n<figure class=\"wp-block-image size-full\"><img decoding=\"async\" src=\"https:\/\/onepress.co.kr\/wp-content\/uploads\/2026\/07\/scn2a-personalized-aso-ko.png\" alt=\"SCN2A \ubcc0\uc774 \uc0ac\ubcf8\uc758 RNA\ub9cc \uc120\ud0dd\uc801\uc73c\ub85c \uc5b5\uc81c\ud558\uace0 \uc815\uc0c1 \uc0ac\ubcf8\uc740 \uc720\uc9c0\ud558\ub294 ASO \uc791\ub3d9 \uc6d0\ub9ac\ub97c \uc124\uba85\ud55c \uc81c\uc791 \uc774\ubbf8\uc9c0\" loading=\"lazy\" \/><figcaption class=\"op-briefing-image-caption\">\uc81c\uc791 \uc774\ubbf8\uc9c0: ONEPRESS\uac00 \ud658\uc790\ubcc4 ASO\uac00 \ubcc0\uc774 \uc720\uc804\uc790 \uc0ac\ubcf8\uc758 \ubc1c\ud604\uc744 \uc120\ud0dd\uc801\uc73c\ub85c \ub0ae\ucd94\ub294 \uc6d0\ub9ac\ub97c \uc124\uba85\ud558\uae30 \uc704\ud574 \uad6c\uc131\ud588\ub2e4. \uc2e4\uc81c \ud658\uc790\ub098 \uce58\ub8cc \uc7a5\uba74\uc774 \uc544\ub2c8\ub2e4.<\/figcaption><\/figure>\n<h2>\ud76c\uadc0\uc9c8\ud658 \uce58\ub8cc\uc758 \ub2e8\uc704\uac00 \uac1c\uc778\uc73c\ub85c \uc881\uc544\uc84c\ub2e4<\/h2>\n<p>\uc774 \uc811\uadfc\uc740 \ud558\ub098\uc758 \uc57d\uc744 \uac19\uc740 \uc9c8\ud658 \uc804\uccb4\uc5d0 \uc4f0\ub294 \ub300\uc2e0 \ud55c \ud658\uc790\uc758 \uc720\uc804\uccb4\uc5d0 \ub9de\ucdb0 \uc57d\uc744 \uc124\uacc4\ud558\uace0 \uc2dc\ud5d8\ud55c\ub2e4. \ubcc0\uc774\uac00 \ub9e4\uc6b0 \ub4dc\ubb3c\uc5b4 \ub300\uaddc\ubaa8 \uc2dc\ud5d8\uc774 \uc5b4\ub824\uc6b4 \uc9c8\ud658\uc5d0\ub3c4 \uac1c\ubc1c \uacbd\ub85c\ub97c \ub9cc\ub4e4 \uc218 \uc788\ub2e4\ub294 \uc810\uc774 \ud575\uc2ec\uc774\ub2e4.<\/p>\n<p>\ubcc4\ub3c4 \uc601\uc544 \ucf54\ud638\ud2b8\uc5d0\uc11c\ub294 \uc57d 16%\uac00 \uac19\uc740 \uc778\uc811 \uc720\uc804 \ud45c\uc9c0 \uc804\ub7b5\uc5d0 \ub9de\ub294 \uac83\uc73c\ub85c \ubd84\uc11d\ub410\ub2e4. \uac00\ub2a5\uc131\uc744 \ubcf4\uc5ec\uc8fc\uc9c0\ub9cc \ubaa8\ub4e0 SCN2A \ud658\uc790\uc5d0\uac8c \ubc14\ub85c \uc801\uc6a9\ub41c\ub2e4\ub294 \ub73b\uc740 \uc544\ub2c8\ub2e4.<\/p>\n<h2>\ud6a8\uacfc\ub97c \uc77c\ubc18\ud654\ud558\uba74 \uc548 \ub418\ub294 \uc774\uc720<\/h2>\n<p>\ub450 \uc2dc\ud5d8 \ubaa8\ub450 \ud658\uc790 \uc790\uc2e0\uc744 \uce58\ub8cc \uc804 \ube44\uad50 \uae30\uc900\uc73c\ub85c \uc0bc\uc558\ub2e4. \ubc1c\ub2ec \ubcc0\ud654\uc5d0\uc11c \ubc1c\uc791 \uac10\uc18c, \ubcd1\uc6a9\uc57d \uc870\uc815, \uc131\uc7a5\uc758 \uc601\ud5a5\uc744 \uc644\uc804\ud788 \ubd84\ub9ac\ud560 \uc218 \uc5c6\uace0 \uc7a5\uae30 \uc548\uc804\uc131\uacfc \ud6a8\uacfc \uc9c0\uc18d\uc131\ub3c4 \ub354 \ud655\uc778\ud574\uc57c \ud55c\ub2e4.<\/p>\n<p>\uc774\ubc88 \uacb0\uacfc\ub294 \uac1c\uc778 \ub9de\ucda4 \uce58\ub8cc\uac00 \uc2e4\uc81c \uc784\uc0c1 \ubcc0\ud654\ub97c \ub9cc\ub4e4 \uc218 \uc788\ub2e4\ub294 \uadfc\uac70\uc774\uc9c0, \uc774\ubbf8 \ub110\ub9ac \uc4f8 \uc218 \uc788\ub294 \ud45c\uc900 \uce58\ub8cc\uac00 \ub410\ub2e4\ub294 \uc758\ubbf8\uac00 \uc544\ub2c8\ub2e4.<\/p>\n<h2>\ub2e4\uc74c \ud655\uc778 \uc9c0\uc810<\/h2>\n<p>\ud6c4\uc18d \ucd94\uc801\uc5d0\uc11c \ubc1c\uc791 \uac10\uc18c\uc640 \ubc1c\ub2ec \ubcc0\ud654\uac00 \uc720\uc9c0\ub418\ub294\uc9c0, \ubc18\ubcf5 \ucc99\uc218\uac15 \ud22c\uc5ec\uc758 \uc7a5\uae30 \uc548\uc804\uc131\uc774 \uc5b4\ub5a4\uc9c0, \uac19\uc740 \uc124\uacc4 \uc6d0\ub9ac\ub97c \ub354 \ub9ce\uc740 \uc720\uc804\uc9c8\ud658\uc5d0 \uc5bc\ub9c8\ub098 \ube60\ub974\uac8c \uc801\uc6a9\ud560 \uc218 \uc788\ub294\uc9c0\uac00 \ub2e4\uc74c \ud310\ub2e8 \uae30\uc900\uc774\ub2e4.<\/p>\n<h2>\uacf5\uc2dd \uc6d0\uc790\ub8cc<\/h2>\n<p><a href=\"https:\/\/pubmed.ncbi.nlm.nih.gov\/42481851\/\" target=\"_blank\" rel=\"noopener noreferrer\">Nature Medicine \/ PubMed original study<\/a><\/p>\n<p><a href=\"https:\/\/radygenomics.org\/2026\/personalized-gene-therapy-helps-teen-with-rare-form-of-severe-epilepsy-walk-independently\/\" target=\"_blank\" rel=\"noopener noreferrer\">Rady Children&#8217;s Institute for Genomic Medicine study release<\/a><\/p>\n<p><a href=\"https:\/\/clinicaltrials.gov\/study\/NCT06314490\" target=\"_blank\" rel=\"noopener noreferrer\">ClinicalTrials.gov NCT06314490<\/a><\/p>\n<p><a href=\"https:\/\/www.cirm.ca.gov\/clinical-trial\/personalized-antisense-oligonucleotide-therapy-for-rare-pediatric-genetic-disease-scn2a\/\" target=\"_blank\" rel=\"noopener noreferrer\">California Institute for Regenerative Medicine trial record<\/a><\/p>\n","protected":false},"excerpt":{"rendered":"<p>SCN2A \uc720\uc804\uc790 \ubcc0\uc774\ub85c \uc911\uc99d \ubc1c\ub2ec\uc131 \ub1cc\uc804\uc99d\uc744 \uc553\ub294 \ub450 \uc544\uc774\uc5d0\uac8c \uac01\uc790\uc758 \ubcc0\uc774 \uc0ac\ubcf8\ub9cc \uaca8\ub0e5\ud55c ASO\ub97c \ud22c\uc5ec\ud55c \uacb0\uacfc, 2\ub144 \ub3d9\uc548 \ubc1c\uc791 \ube48\ub3c4\uac00 \uac01\uac01 26%\uc640 90% \uc904\uc5c8\ub2e4. \ud658\uc790\uac00 \ub450 \uba85\ubfd0\uc778 \ucd08\uae30 \uac1c\ubcc4 \uc784\uc0c1\uc2dc\ud5d8\uc774\ub77c\ub294 \ud55c\uacc4\ub3c4 \ud568\uaed8 \ubd10\uc57c \ud55c\ub2e4.<\/p>\n","protected":false},"featured_media":0,"template":"","meta":[],"class_list":["post-836","briefing","type-briefing","status-publish","hentry"],"_links":{"self":[{"href":"https:\/\/onepress.co.kr\/index.php\/wp-json\/wp\/v2\/briefing\/836","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/onepress.co.kr\/index.php\/wp-json\/wp\/v2\/briefing"}],"about":[{"href":"https:\/\/onepress.co.kr\/index.php\/wp-json\/wp\/v2\/types\/briefing"}],"wp:attachment":[{"href":"https:\/\/onepress.co.kr\/index.php\/wp-json\/wp\/v2\/media?parent=836"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}